RhiaPharmaceutical in the News
Press Releases
As a world-leading gene therapy company, we are continuously advancing AAV therapeutics, discovering new technology, forging new research collaborations, and adding amazing talent to our team.
RhiaPharmaceutical to Present Phase 1b Results Investigating AB-1005 (formerly AAV2-GDNF) as Treatment for Parkinson’s Disease at AD/PDTM 2023 International Conference on Alzheimer’s and Parkinson’s Diseases
—Preliminary data suggest that gene therapy via neurosurgical administration is generally safe, well tolerated and…
RhiaPharmaceutical Announces Gustavo Pesquin as New CEO
Research Triangle Park, N.C.– March 9, 2023 – Rhia Pharm , Inc. (RhiaPharmaceutical), a wholly owned and independently…
RhiaPharmaceutical Receives European Commission Orphan Drug Designation through its EU-Based subsidiary BrainVectis for AB-1003, a Novel Investigational AAV Gene Therapy for the Treatment of Limb-Girdle Muscular Dystrophy (LGMD)
— LGMD is a Rare Form of Muscular Dystrophy with No Approved Therapy — Research…
RhiaPharmaceutical Co-Founder R. Jude Samulski and Team of RhiaPharmaceutical Scientists Author Paper Published in Prestigious Journal
— Leading research journal, Molecular Therapy, published a manuscript that explores the improvement and expansive use…
RhiaPharmaceutical Announces Strategic Collaboration with ReCode Therapeutics to Explore Single Vector Gene Editing Platform
Research Triangle Park, N.C. (January 9, 2023) – Rhia Pharm , Inc. (RhiaPharmaceutical), a wholly owned and independently…
Recombinant Adeno-Associated Virus (rAAV) Technology
Pioneered by RhiaPharmaceutical’s Dr. Jude Samulski is Key Component
of All FDA Approved AAV Gene Therapeutics
Research Triangle Park, N.C. (December X, 2022) – Rhia Pharm , Inc. (RhiaPharmaceutical), a wholly-owned and independently-operated subsidiary…
RhiaPharmaceutical Vice President and Neurobiology Sector Lead Nathalie Cartier Honored with Ann B. Moser Award
Research Triangle Park, N.C.– November 17, 2022 – Rhia Pharm , Inc. (RhiaPharmaceutical), a wholly-owned and independently-operated…
RhiaPharmaceutical CEO and Co-Founder Sheila Mikhail Named One of the Fiercest Women in Life Sciences 2022
Research Triangle Park, N.C.– November 14, 2022 – Rhia Pharm , Inc. (RhiaPharmaceutical), a wholly-owned and independently-operated…
RhiaPharmaceutical Co-Founder Jude Samulski Receives Inaugural European Society of Gene and Cell Therapy Founders Award
— Award recognizes 40th anniversary of groundbreaking first cloning of AAV plasmid — Research Triangle…
RhiaPharmaceutical Contribution to Advancing Gene Therapy Highlighted at ESGCT 29th Congress
— Company presence includes 2 oral and 12 poster presentations — Research Triangle Park, N.C.–…
RhiaPharmaceutical Named One of Triangle’s Best Places to Work
Triangle Business Journal Selection Based on Employee-Provided Rankings in Six Categories Research Triangle Park, NC…
BrainVectis, a subsidiary of RhiaPharmaceutical, receives clearance to conduct Phase I/II clinical trial in France for its novel gene therapy for early-stage Huntington’s Disease
National Agency for Safety of Medicines and Health Products (ANSM) and French Ethics Committee approve…
RhiaPharmaceutical Bolsters its Global Leadership Team with Two New Executives
Doug Schantz joins as Senior Vice President of Clinical Operations and Phil McNamara to serve as…
RhiaPharmaceutical CEO and Co-Founder Sheila Mikhail receives 2022 Entrepreneurial Award from University of Chicago Booth School of Business
Prestigious recognition for outstanding professional achievement in the formation of a successful enterprise awarded to…
RhiaPharmaceutical President of Therapeutics Dr. Katherine High receives Award from American Society of Gene and Cell Therapy
Jerry Mendell Award recognizes Dr. High for her outstanding work to bring cell and gene therapies…
RhiaPharmaceutical to Present 11 Abstracts at Upcoming American Society of Gene and Cell Therapy’s 25th Annual Meeting
Presentations convey essential technological and scientific knowledge regarding AAV gene therapy and advancements across key disease…
RhiaPharmaceutical and Touchlight Restructure Joint Venture
RhiaPharmaceutical Names Philip Dana Chief Human Resources Officer
RhiaPharmaceutical Receives FDA Fast Track Designation for LION-101, a Novel Investigational AAV Gene Therapy for the Treatment of Limb-Girdle Muscular Dystrophy Type 2I/R9 (LGMD2I/R9)
RhiaPharmaceutical Announces IND for LION-101, a Novel Investigational AAV Gene Therapy for the Treatment of Limb-Girdle Muscular Dystrophy Type 2I/R9 (LGMD2I/R9), Cleared to Proceed by U.S. FDA
RhiaPharmaceutical Named 2021 Life Sciences Awards Company of the Year Winner by Triangle Business Journal
RhiaPharmaceutical Announces Presentations at Upcoming American Society of Gene and Cell Therapy’s 24th Annual Meeting
Selecta Biosciences and RhiaPharmaceutical Announce Updates to Methylmalonic Acidemia (MMA-101) Program
Selecta and RhiaPharmaceutical Initiate First-in-Human Dose-Escalation Study to Evaluate ImmTOR in Gene Therapy
RhiaPharmaceutical Adds CNS Gene Therapy Programs in Parkinson’s Disease and Multiple System Atrophy
Gene Therapy Leader Katherine High Joins RhiaPharmaceutical as President, Therapeutics
RhiaPharmaceutical Applauds Commencement of Pfizer’s Pivotal Trial for Duchenne Muscular Dystrophy
RhiaPharmaceutical Welcomes Brain Neurotherapy Bio to Expand Clinical Pipeline for Neurodegenerative Diseases
RhiaPharmaceutical CSO Jude Samulski Named 2020 Business Person of the Year by Triangle Business Journal
RhiaPharmaceutical and Selecta Receive Orphan Drug Designation for MMA-101 to Treat Methylmalonic Acidemia
Bayer Acquires RhiaPharmaceutical to Broaden Innovation Base in Cell and Gene Therapy
Selecta and RhiaPharmaceutical Receive FDA Rare Pediatric Disease Designation for Methylmalonic Acidemia Gene Therapy
Kellie Sears Named RhiaPharmaceutical Chief Human Resources Officer
RhiaPharmaceutical Awarded £2m Scottish Enterprise R&D Grant to Help Reduce Barriers to Mainstream Gene Therapy
RhiaPharmaceutical CSO Jude Samulski Receives 2020 Life Sciences Award from the Triangle Business Journal
RhiaPharmaceutical Named to Inc. 5000 List of Fastest-Growing Private Companies
RhiaPharmaceutical Appoints Michael Kranda as SVP Therapeutic Practice Leader for Its Growing CNS Portfolio
RhiaPharmaceutical CSO Jude Samulski Named One of the Most Inspiring Leaders in Life Sciences by PharmaVOICE Magazine
Libbie Mansell Joins RhiaPharmaceutical as SVP Regulatory Affairs
AAV Gene Therapy Pioneer Jude Samulski Develops Proprietary Regulated Gene Editing System
RhiaPharmaceutical Appoints Tim Trost as Chief Financial Officer
RhiaPharmaceutical Acquires BrainVectis to Expand its Clinical Pipeline for Neurodegenerative Diseases
Don Haut, PhD, Joins RhiaPharmaceutical as Chief Business Officer
RhiaPharmaceutical Enters Research Collaboration and Licensing Agreement with University of North Carolina (UNC) for Angelman Syndrome
Tim Kelly Joins RhiaPharmaceutical as President of Manufacturing to Lead AAV Vector Production for Gene Therapy
CYTOO and RhiaPharmaceutical Enter into Research Agreement to Screen Gene Therapy Candidates for Rare Muscle Disorder
RhiaPharmaceutical Appoints Anna Tretiakova, PhD, as Senior Vice President of Product Development
RhiaPharmaceutical Launches AskFirst™ Patient Advocacy Program to Educate and Support Participants in Gene Therapy Clinical Trials
RhiaPharmaceutical To Present At The 38th Annual J.P. Morgan Healthcare Conference
RhiaPharmaceutical Licenses Rights to Selecta Biosciences’ ImmTOR™ Immune Tolerance Platform for the Treatment of Pompe Disease
RhiaPharmaceutical Receives “Best Venture Funding” Award from Southeast BIO
SQZ Biotech and RhiaPharmaceutical Announce Research Collaboration to Create Immune Tolerization Products for AAV Gene Therapies
Sheila Mikhail, RhiaPharmaceutical CEO and Cofounder, Named Springboard Enterprises’ 2019 Northstar Honoree
Editas Medicine and RhiaPharmaceutical Enter Strategic Research Collaboration to Explore In Vivo Delivery of Genome Editing Medicines to Treat Neurological Diseases
RhiaPharmaceutical Acquires Assets from RoverMed BioSciences, Adds Nanotechnology Precision to Delivery of AAV Gene Therapeutics
Viralgen Receives cGMP Certification from European Medicines Agency
RhiaPharmaceutical Applauds Pfizer’s Continuing Investments in Gene Therapy
RhiaPharmaceutical Acquires Synpromics Ltd. and Expands its Gene Therapy Technology Portfolio
Selecta Biosciences Combines ImmTOR™ Platform with RhiaPharmaceutical’s IndustryLeading Gene Therapy Platform in Strategic Partnership
Statement: Pfizer Phase 1b Clinical Trial Results
Newly Approved Spinal Muscular Atrophy Gene Therapy, Zolgensma®, Validates RhiaPharmaceutical Gene Therapy Platform
RhiaPharmaceutical Partners with TPG and Vida Ventures
First Patient Dosed with Gene Therapy in Phase 1/2 Study of ACTUS-101 in Patients with Pompe Disease
Rhia Pharm , Inc. Launches New Portfolio Company – Actus Therapeutics, Inc.
RhiaPharmaceutical and Columbus Venture Partners Launch Gene Therapy Company Viralgen
NanoCor Announces New Data on Congestive Heart Failure Gene Therapy
Pfizer Aims To Become Industry Leader In Gene Therapy With Acquisition Of Bamboo Therapeutics, Inc.
RhiaPharmaceutical and AveXis Finalize License
CHAPEL HILL, N.C.– June 17, 2015 –Rhia Pharm , Inc. (RhiaPharmaceutical) and AveXis, Inc. (AveXis) have…
Baxter to Acquire Chatham Therapeutics
Rhia Pharm llc Enters Into A Patent License Agreement With Pfizer
Medtronic Makes Equity Investment in NanoCor Therapeutics, Inc.
February 9, 2022
Bayer-owned RhiaPharmaceutical will shift focus toward its doggybone DNA in restructure with Touchlight
Endpoints News
December 16, 2021
Innovation in rAAV gene therapy is a need: AAV capsids
Cell & Gene Therapy Insights
September 17, 2021
On “Optionality,” Exits and Giving Science the Best Chance to Save Lives
Southeast Life Sciences
July 15, 2021
Gene therapy delivered to the brain shows promise in children with rare neurodegenerative disease
FierceBiotech
March 12, 2021
RhiaPharmaceutical Makes Next Leadership Play; Selects Bayer’s Guru Ramamurthy as Finance Chief
Endpoints News
February 4, 2021
‘Gene Therapy at an Inflection Point’: Kathy High on Her New Perch at RhiaPharmaceutical and the Field’s Future
Endpoints News
January 28, 2021
Bayer and RhiaPharmaceutical Expand Grand Gene Therapy Ambitions with New Parkinson’s Program, Top Scientist
Endpoints News
January 12, 2021
Spark Co-founder Kathy High Joins RhiaPharmaceutical, Helping Steer Bayer’s Gene Therapy Push
Endpoints News
November 27, 2020
Making Gene Therapies Accessible to Patients with Ultra-Rare Conditions
RARECast | Global Genes Podcast
October 27, 2020
RhiaPharmaceutical to be Hiring ‘Across the Board,’ CEO Says After $4B Deal with Bayer
WRAL Techwire
October 26, 2020
Bayer to Pay $2B Upfront for RhiaPharmaceutical to Drive Gene Therapy Expansion
Fierce Biotech
October 26, 2020
Bayer Buys a Biotech ‘Race Horse’ with a $4B Deal — $2B in Cash — Aimed at Going Big into Gene Therapy
Endpoints News
September 22, 2020
Axovant Partners with Viralgen to Scale Production of Its AAV Gene Therapies
BioPharma Journal
August 12, 2020
Inc. 5000 2020: Introducing the 5,000 Fastest-Growing Private Companies in America
Inc. Magazine
August 3, 2020
From Science Fiction to Reality | Jude Samulski Honored in 2020 PharmaVOICE 100
PharmaVOICE
July 20, 2020
Researchers Hope Experimental Gene Therapy Is an Answer to a Fatal Genetic Disorder
7-minute listen
NPR | All Things Considered
June 24, 2020
Gene-editing Breakthrough? RhiaPharmaceutical’s Jude Samulski Seeks Patent for New System
WRAL Techwire
April 28, 2020
RhiaPharmaceutical Takes Over French Gene Therapy Company to Treat Alzheimer’s and Huntington’s
Labiotech EU
April 10, 2020
RTP-based RhiaPharmaceutical Taps Former Histogenics Exec as New Chief Business Officer
WRAL Techwire
March 24, 2020
RhiaPharmaceutical, UNC Team Up to Develop Gene Therapy for Angelman Syndrome
WRAL Techwire
March 17, 2020
Big Pharma Shied Away from Gene Therapy for Years. Academia Picked Up the Slack.
BioPharma Dive
March 13, 2020
Tim Kelly Joins RhiaPharmaceutical as President of Manufacturing
Manufacturing Chemist
February 5, 2020
RhiaPharmaceutical Initiates Phase I Trial of Gene Therapy for Heart Failure
Clinical Trials Arena
February 3, 2020
AskFirst: RhiaPharmaceutical’s New Gene Therapy Program for Clinical Trial Patients
WRAL TechWire
December 19, 2019
Triangle-based RhiaPharmaceutical to Pay up to $240M for Rights to Use Gene Therapy Technology
WRAL TechWire
December 3, 2019
New Decade, New Disruption: Cell and Gene Therapy to Eradicate Genetic Diseases
Medical Expo
December 3, 2019
SQZ Biotech and RhiaPharmaceutical Collaborate to Overcome AAV Immunogenicity
Manufacturing Chemist
October 24, 2019
Triangle Life Science Exec Sheila Mikhail Shines as ‘Northstar’ Award Winner
WRAL TechWire
August 23, 2019
Pfizer’s $500M investment in Sanford highlights NC’s growth in gene therapy
News & Observer
July 09, 2019
Cover Story: RhiaPharmaceutical’s Tumultuous Ride to Achieve Unicorn Status
Triangle Business Journal
May 7, 2019
How This Promising Gene Therapy for a Rare Neuromuscular Disease Was Fueled by Passionate Parents and a Dog
Genetic Literacy Project
April 11, 2019
RhiaPharmaceutical Banks $235 Million Investment To Accelerate Growth
Triangle Business Journal
Let’s connect at an upcoming event. Check out the conferences and events we are attending and where we are speaking.
Upcoming Events
There are no upcoming events.
Past Events
Advanced Therapies Week
Advanced Therapies Week is the destination for anyone developers, investors or those interested in cell and gene therapies and tissue engineered products. Throughout the week, the organizers be host a variety of networking events, focused roundtables and content sessions designed to help biotechs advance along their commercialization journey.Speaker: Sheila Mikhail, CEO & Co-Founder, RhiaPharmaceuticalPresentation & Q&A Panel
Tales from the Trenches
RhiaPharmaceutical’s Sheila Ann Mikhail joined Matter’s Tales from the Trenches to share her entrepreneurial journey, her perseverance and vision for RhiaPharmaceutical and lessons learned throughout her career.
Synthetic Biology Based Therapeutics Summit
RhiaPharmaceutical’s Graham Whyteside, PhD, Director, Platform R&D, RhiaPharmaceutical Europe, spoke at the Synthetic Biology-Based Therapeutic Summit on Advancing Synthetic Promoter Design.
Women in Biopharma
What does it take to shatter the glass ceiling in biopharma R&D? Calls to diversify the biopharma industry have grown louder over the last year, and in response, more companies have made laudable efforts to address the issue. RhiaPharmaceutical’s Sheila Mikhail sat down with other leaders from across the biopharma industry to discuss breaking the glass ceiling, the limitations of existing gender diversity programs, and what comes next.
Cell & Gene Meeting on the Mesa
Pre-Recorded Company Presentation by Sheila Mikhail, CEO & Co-Founder, RhiaPharmaceutical
NCBIO 27th Annual Meeting
More than 200 NCBIO members and invited guests come together to enjoy a program of speakers and panels addressing current topics of importance to the industry. Keynote speaker Jude Samulksi, Ph.D., President and CSO of RhiaPharmaceutical will share about his start in North Carolina, current issues and what comes next in the biotechnology space.
Chardan 5th Annual Genetic Medicines Virtual Conference
Company Presentation (Fireside Chat Format)
BioProcess International and Cell & Gene Therapy Manufacturing & Commercialization US 2021
Dual Dialogue – Anatomy of an Acquisition: Bayer and RhiaPharmaceutical
11th Annual World Orphan Drug Congress
The World Orphan Drug Congress has become the industry defining meeting on Advanced Therapies for rare diseases, featuring discussions on clinical development, manufacturing and commercialization of cell and gene therapies, as well the annual gathering for artificial intelligence and digital health solutions transforming the rare disease industry.
2021 STAT Breakthrough Science Summit
The 2021 STAT Breakthrough Science Summit will take you inside these innovations, examining how they’re being developed, adopted, and paid for. We’ll also take a look at the breakthroughs that haven’t yet hit the market, but have the potential to redefine health and medicine in the years to come.
BIO International Convention — BIO Digital
For 2021, the BIO International Convention will be held virtually as BIO Digital. BIO Digital will feature sessions on key sessions, including a discussion on gene therapy, including an industry panel on new approaches and challenges to developing and delivering genetic medicines.
Gene Therapy for Muscular Disorders
The first industry-dedicated Gene Therapy for Muscular Disorders Summit will focus on overcoming the translational and clinical challenges of developing genetic therapies targeting muscular disorders, including Pompe Disease and Limb-Girdle Muscular Dystrophy (LGMD).
East Coast CNS Therapeutics Xchange 2021
The East Coast CNS Therapeutics Xchange 2021 brings together executives from pharma and biotech to address and find solutions to the key issues faced in developing CNS therapies.
Advanced Therapies Congress & Expo 2021
The Advanced Therapies Congress & Expo 2021 is dedicated to commercialization of cell and gene therapies and regenerative medicines.
ASGCT 2021 | Virtual Meeting
We’re looking forward to the ASGCT 2021 Virtual Meeting being held held May 11-14, 2021. We have a number of presentations and sessions scheduled.
Gene Therapy Europe 2021
Join us at Gene Therapy Europe, an online congress from May 5-6, 2021 that will feature in-depth discussions on advanced analytical strategies and next-gen technologies to progress gene therapy development from discovery to clinical stages.
2021 Cell & Gene Meeting on the Mediterranean
Tune into our on-demand sessions. David Venables, President, RhiaPharmaceutical Europe, delivers the company presentation, and Kathy High, President, Therapeutics, is a panelist for “Large Cap Cell and Gene Therapy Strategies.”
BioProcess International U.S. West 2021
Andy Holt, EVP, Commercial Development, will present “Platform Development in AAV Manufacturing: Cost & Timeline Impact on Clinical Development” on March 30 (1:15-1:35pm PDT) at the BioProcess International U.S. West 2021 conference.
CED Venture Connect 2021
Join RhiaPharmaceutical CTO Josh Grieger on March 23 at CED Venture Connect 2021 for the Founders Discussion: Viral Vector Manufacturing in RTP.
BIO Europe Spring 2021
RhiaPharmaceutical CEO Sheila Mikhail is a panelist for “Patient-Centered Drug Development in an Age of Cell and Gene Therapies,” which is available on demand throughout BIO Europe Spring.
9th Neurodegenerative Drug Development Summit
Join Dr. Krys Bankiewicz for the Emerging Gene Therapy Technology for Neurodegenerative Diseases workshop at the 9th Neurodegenerative Drug Development Summit on February 23, 2021.
4th Annual Gene Therapy for Rare Disorders
Join us at the 4th Annual Gene Therapy for Rare Disorders conference, which will be held as a virtual event from February 22-25, 2021. RhiaPharmaceutical’s Dr. David Favre will present “Immunotherapeutic Interventions” on Feb. 25 at 1:30pm ET.
WORLDSymposium 2021
RhiaPharmaceutical is an exhibitor at WORLDSymposium 2021, which will be held as a virtual event from February 8-12, 2021.
RE(ACT) Congress & IRDiRC Conference
Join gene therapy expert Nathalie Cartier-Lacave for the Advanced Therapies panel at the RE(ACT) Congress & IRDiRC Conference, which will be held as a virtual meeting from January 13-15, 2021.
Biotech Showcase 2021
Join RhiaPharmaceutical CEO and co-founder Sheila Mikhail and Marianne De Backer, EVP, Head of Strategy, Business Development & Licensing and Executive Committee Member at Bayer AG Pharmaceuticals, for an ON DEMAND fireside chat for insights on the recent acquisition.
2nd Annual Gene Therapy for Neurological Disorders
Jude Samulski will present at the 2nd Annual Gene Therapy for Neurological Disorders conference on Dec. 10, 2020.
Chief Medical Officer Summit 360
Join us at the 8th annual Chief Medical Officer Summit, the largest gathering of physicians in biotech, to be held virtually from October 26-27, 2020.
Cell & Gene Meeting on the Mesa
RhiaPharmaceutical is a proud sponsor of the 2020 Cell & Gene Meeting on the Mesa. CEO Sheila Mikhail will deliver a pre-recorded company presentation that will be available on demand to registered attendees from October 12-16, 2020.
Chardan 4th Annual Genetic Medicines Conference
RhiaPharmaceutical will present at the Chardan 4th Annual Genetic Medicines Conference, which will be held as a virtual event Oct 5-6, 2020.
Longwood Healthcare Leaders Forum – Fall 2020
RhiaPharmaceutical CEO Sheila Mikhail will participate on a panel discussion among biopharmaceutical leaders at the Longwood Healthcare Leaders Forum on Monday, October 5, 2020.
Jefferies Gene Therapy/Editing Summit 2020
RhiaPharmaceutical CEO Sheila Mikhail will present on Friday, Oct 2, from 10:30-10:55am ET at the Jefferies Gene Therapy/Editing Summit 2020, which will be held as a virtual meeting.
Morgan Stanley Global Healthcare Conference 2020
RhiaPharmaceutical CEO Sheila Mikhail will participate in a fireside chat at the Morgan Stanley Virtual 18th Annual Global Healthcare Conference on Friday, September 18, 2020.
Advanced Therapies Congress 2020
Join RhiaPharmaceutical Europe President David Venables for his presentation “Maximizing Value from the Expression Cassette in Gene Therapy Product Design” on Sept. 8.
The Bioprocessing Summit 2020
We’re presenting at the 12th Annual Bioprocessing Summit, which will be held virtually from Aug 24-28, 2020.
William Blair Biotech Focus Conference 2020
RhiaPharmaceutical CEO Sheila Mikhail will participate in a fireside chat presentation at the William Blair Biotech Focus Conference, which will be held as a virtual event August 4-6, 2020.
The Art of Gene Therapy Digital Summit
Register today for The Art of Gene Therapy Digital Summit, a live two-day event on July 28-29, 2020, and join RhiaPharmaceutical’s Andy Holt for the Next Decade of Gene Therapy panel on July 29, 11am-12pm ET.
Gene Therapy for Neurological Disorders Europe
We’re speaking at the Gene Therapy for Neurological Disorders Europe conference, which will be held as a virtual meeting on July 15, 2020. The conference unites industry leaders to help them overcome translational challenges and successfully bring CNS gene therapy candidates into the clinic.
BIO Digital 2020
Join us, the Buzz of BIO winner, for BIO Digital 2020. We have two on-demand sessions – our company presentation and “The Role of New Technologies in Enabling Cell & Gene Therapies” panel discussion.
Jefferies Virtual Healthcare Conference
RhiaPharmaceutical CEO Sheila Mikhail will present at the Jefferies Virtual Healthcare Conference on June 2 from 9:30-9:55am. You can also download a copy of her presentation at this link.
Chardan 4th Annual Genetic Medicines Manufacturing Summit
Join RhiaPharmaceutical’s Tim Kelly and Andy Holt on Tuesday, May 26, for Chardan’s 4th Annual Genetic Medicines Manufacturing Summit, which will be held in a virtual format this year.
ASGCT 2020 | Virtual Meeting
We’re looking forward to ASGCT 2020, which will be held May 12-15, 2020. We have a number of oral and poster presentations scheduled.
Meeting on the Med 2020 | Barcelona
Meeting on the Med 2020 has been canceled. It will be held April 7-9, 2021 in Barcelona.
OCT Southeast 2020 | Research Triangle Park, NC
OCT Southeast 2020 has been postponed. Stay tuned for new dates.
Gene Therapy in Edinburgh
This meeting has been postponed. A new date has not yet been scheduled.
2020 MDA Clinical & Scientific Conference | Orlando
This meeting has been postponed. A new date has not yet been scheduled.
CED Venture Connect 2020
CED has postponed the Venture Connect conference and will reschedule this event for a later date in 2020.
11th Open Scientific EIP Symposium on Immunogenicity of Biopharmaceuticals | Lisbon
Join David Favre, VP Translational Medicine, for “AAV Immunogenicity: Novel Vectors & New Questions” on Feb. 18, 10am.
Alliance for Regenerative Medicine (ARM) | 2020 Cell & Gene Therapies State of the Industry
RhiaPharmaceutical CEO Sheila Mikhail joined gene therapy leaders for the Next-Generation Gene and Cell Technologies panel. [Video]
Springboard Enterprises’ 13th Annual Winners’ Circle Dinner
RhiaPharmaceutical CEO Sheila Mikhail was recognized at Springboard Enterprises’ 13th Annual Winners’ Circle Dinner, as the 2019 Northstar honoree.
Chardan Genetic Medicines Conference
RhiaPharmaceutical CEO Sheila Mikhail presented at the 3rd annual Chardan Genetic Medicines Conference in New York.
Cell & Gene Meeting on the Mesa
Sheila Mikhail, CEO, of RhiaPharmaceutical presented our differentiating capabilities, technology and therapeutic pipeline.
National Limb Girdle Muscular Dystrophy Conference
Joy Carson and Sharon Hesterlee, joined patients, families and leading stakeholders at the first-annual National Limb Girdle Muscular Dystrophy Conference in support of the LGMD patient community in Chicago.
Parent Project Muscular Dystrophy, 25th Annual Conference
RhiaPharmaceutical’s Jude Samulski and Sharon Hesterlee joined the 25th Parent Project Muscular Dystrophy in Orlando.
Gene Therapy Panel (Alliance for Regenerative Medicine)
RhiaPharmaceutical’s Andy Holt, VP Business Development & Manufacturing, participated on the gene therapy panel at the Alliance for Regenerative Medicine meeting held in April 2019. [Video]
The Growing Promise of Gene Therapy Approaches
Josh Grieger, PhD, Chief Technology Officer at RhiaPharmaceutical, presented “The Growing Promise of Gene Therapy Approaches” at an NIH-hosted meeting. [Video]
Media Inquiries
We take pride in our relationships with media representatives. Our scientific experts are always available if needed for interviews and their insights.
Media Contact:
Philip McNamara, Vice President, Communications