ASGCT 2020 | Virtual Meeting

We’re looking forward to the ASGCT 2020 Annual Meeting, which will be a virtual conference held May 12-15, 2020. We have a number of oral and poster presentations scheduled.

ORAL PRESENTATIONS

Adeno-Associated Virus Evolution from “Almost a Virus” to “An Amazing Vector”
Presenter:  Jude Samulski, PhD, UNC Gene Therapy Vector Core, RhiaPharmaceutical
Tuesday, May 12, 2020
Main Session:  The Golden Age of Gene Therapy:  Past, Present & Future Perspectives
Presentation Time:  8:00am – 8:26am ET

Phase 1 Study of Gene Therapy in Late-Onset Pompe Disease: Analyses of Safety and Secondary Endpoints
Presenter:  Dwight Koeberl, MD, PhD, Duke University School of Medicine
Wednesday, May 13, 2020
Main Session:  AAV Vectors – Clinical Studies II
Presentation Time:  5:15pm – 5:30pm ET
Abstract number:  509

AAV Capsid-Promoter Interactions Determine CNS Cell-Selective Gene Expression In Vivo
Presenter:  Sara Powell, PhD, RhiaPharmaceutical
Wednesday, May 13, 2020
Session Title:  Controlling AAV Gene Expression: Shifting Paradigms
Presentation Time: 4:00pm – 4:15pm ET
Abstract number: 511

POSTER PRESENTATIONS

Tuesday, May 12, 2020

Full or Empty: A CMC Perspective on Production and Purification of Empty Vector Particles
Presenter:  Paul Greback-Clarke, RhiaPharmaceutical
Session Title:  Vector and Cell Engineering, Production or Manufacturing
5:30pm – 6:30pm ET
Abstract number: 465

Wednesday, May 13, 2020

Development and Validation of a CE-SDS Method for Purity Determination of AAV8
Presenter:  Jeremy Johnston, MS, RhiaPharmaceutical
Session Title:  AAV Vectors – Virology and Vectorology
5:30pm – 6:30pm ET
Abstract number: 554

Development of a Molecular Switch to Regulate Cas9 Expression
Presenter:  Bikash Shakya, PhD, RhiaPharmaceutical
Session Title:  Gene Targeting and Gene Correction
5:30pm – 6:30pm ET
Abstract number: 644

Thursday, May 14, 2020

Novel Machine Learning Algorithms Improve the Design of Synthetic Promoters Resulting in More Selective and Higher Levels of Gene Expression in Muscle and Liver Cells
Presenter:  Michael Roberts, PhD, RhiaPharmaceutical
Session Title:  AAV Vectors – Virology and Vectorology
5:30pm – 6:30pm ET
Abstract number:  1003

Development of Novel Synthetic Promoters for CNS Gene Therapy
Presenter:  Riccardo Privolizzi, PhD candidate, University College of London
Session Title:  Vector and Cell Engineering, Production or Manufacturing
5:30pm – 6:30pm ET
Abstract number:  1262